Does PCORI fund projects regarding newborn screening or treatment options for rare diseases?

PCORI does not fund studies that propose to develop a new screening tool or establish efficacy for a treatment option for any disease. However, if there is a patient-centered CER question related to screening or treatment options for patients with rare disease, it may be of interest to PCORI. The investigator is encouraged to speak with a Program Officer regarding their idea(s) prior to submitting a Letter of Intent. To contact PCORI regarding a research idea, please email pfa@pcori.org.